Guangping Gao
Reproducibility track record
1
assessed papers
84/100
mean reproducibility
1
reproduced (C1–C2)
0
flagged
29
total citations
flag rate:
0%
(0/1)
The share of this author’s assessed papers carrying a ⚑ flag. A concentration is a prompt for expert review — never, on its own, a determination about the person.
Authorship role
first author: 0
last author: 0
Topics
Funders
—
Frequent co-authors
Christine Q. Simmons 1Markus Terrey 1Alexander A. Sousa 1Alfred L. George 1Natalia S. Morsci 1Jun Xie 1Emmanuel Roze 1Laura Anderson 1Cathleen Lutz 1Fabian Suri‐Payer 1
Institutions
Broad Institute 1Jackson Laboratory 1Northwestern University 1Massachusetts General Hospital 1Project HOPE 1University of Massachusetts Chan Medical School 1
Geography (author institutions)
US 1FR 1
Co-author network
Collaborators, sized by shared output and coloured by their own reproducibility (green = high, red = low). Click a node to open their card. A pattern is a prompt for review, never a determination.
How this author’s assessed papers reproduced — the outcome of reproduction attempts, not a judgement of the person. Coverage is partial and grows over time.
Assessed papers (1)
Complete publication record (503)
Request a reproduction →1 assessed by us (1 reproduced) · 502 not yet assessed — every PubMed paper on record, linked below.
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Bta-miR-146b promotes infectious bovine rhinotracheitis virus replication and inhibits type I interferon expression via targeting IRAK1 ↗Frontiers in Cellular and Infection Microbiology · 2026 · PMID 41660427not yet assessed
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An improved method for high-purity isolation of oligodendrocytes from neonatal and adult mouse brain ↗iScience · 2026 · PMID 42111178not yet assessed
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USP24-dependent STAT2 stabilization mediates physiologic and pathologic bone formation ↗Cell Death and Disease · 2026 · PMID 42218160not yet assessed
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Control of lipid metabolism in chondrocytes is critical for skeletal growth ↗Proceedings of the National Academy of Sciences · 2026 · PMID 42224593not yet assessed
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Intravenous administration of an engineered AAV9-gene-silencing vector suppresses human SOD1 and extends survival in an ALS mouse model ↗Nature Communications · 2026 · PMID 42350385not yet assessed
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Long-term depletion of KIR3DL01+ NK cells by adeno-associated viral-vectored antibody delivery alters chronic SIV infection ↗PLoS Pathogens · 2026 · PMID 42555626not yet assessed
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In vivo adenine base editing ameliorates Dravet syndrome phenotypes in a mouse model ↗Science Translational Medicine · 2026 · PMID 42127220not yet assessed
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Long-term comparative analysis of AAV9-mediated gene replacement therapies for spinal muscular atrophy in mice ↗Nature Communications · 2026 · PMID 42177183not yet assessed
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Current clinical applications of AAV-mediated gene therapy ↗Molecular Therapy · 2025 · PMID 40329530not yet assessed
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A comprehensive atlas of AAV tropism in the mouse ↗Molecular Therapy · 2025 · PMID 39863928not yet assessed
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In vivo prime editing rescues alternating hemiplegia of childhood in miceCell · 2025 · PMID 40695277L1 84/100
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The curious case of AAV immunology ↗Molecular Therapy · 2025 · PMID 40156190not yet assessed
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Base editing of trinucleotide repeats that cause Huntington’s disease and Friedreich’s ataxia reduces somatic repeat expansions in patient cells and in mice ↗Nature Genetics · 2025 · PMID 40419681not yet assessed
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Rhodoquinone carries electrons in the mammalian electron transport chain ↗Cell · 2025 · PMID 39909039not yet assessed
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Comprehensive Review of Osteogenesis Imperfecta: Current Treatments and Future Innovations ↗Human Gene Therapy · 2025 · PMID 39932815not yet assessed
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Determinants of successful AAV-vectored delivery of HIV-1 bNAbs in early life ↗Nature · 2025 · PMID 40739359not yet assessed
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AAVone: A cost-effective, single-plasmid solution for efficient AAV production with reduced DNA impurities ↗Molecular Therapy — Nucleic Acids · 2025 · PMID 40503174not yet assessed
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BCKDHA-BCKDHB digenic gene therapy restores metabolic homeostasis in two mouse models and a calf with classic maple syrup urine disease ↗Science Translational Medicine · 2025 · PMID 40009698not yet assessed
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Adeno-associated viral delivery of Env-specific antibodies prevents SIV rebound after discontinuing antiretroviral therapy ↗Science Immunology · 2025 · PMID 40020046not yet assessed
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Transient rapamycin treatment avoids unwanted host immune responses toward AAV-delivered anti-HIV antibodies ↗Nature Communications · 2025 · PMID 41057323not yet assessed
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Adeno-associated Virus-mediated Silencing of Sox4 Leads to Long-Term Amelioration of Liver Phenotypes in Mouse Models of Alagille Syndrome ↗Gastroenterology · 2025 · PMID 40446945not yet assessed
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Nature-inspired IL-1 targeted therapy to treat chronic inflammatory diseases ↗Molecular Therapy · 2025 · PMID 40931517not yet assessed
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miR-375 protects against acetaminophen-induced acute liver failure by orchestrating pharmacogene expression ↗Molecular Therapy · 2025 · PMID 40598772not yet assessed
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GFP-on mouse model for interrogation of in vivo gene editing ↗Nature Communications · 2025 · PMID 40744920not yet assessed
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A single amino acid variant in the variable region I of AAV capsid confers liver detargeting ↗PLoS Pathogens · 2025 · PMID 40961169not yet assessed
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Gene therapy delivery of anti-Müllerian hormone in prepubertal female domestic cats induces long-term sterilization ↗Nature Communications · 2025 · PMID 41315264not yet assessed
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Cell-penetrating peptide-grafted AAV2 capsids for improved retinal delivery via intravitreal injection ↗Molecular Therapy — Methods & Clinical Development · 2025 · PMID 40027263not yet assessed
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Single-cell transcriptomic analyses provide insights into the tumor microenvironment heterogeneity and invasion phenotype in retinoblastoma ↗Pathology - Research and Practice · 2025 · PMID 40378583not yet assessed
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A compact base editor rescues AATD-associated liver and lung disease in mouse models ↗Molecular Therapy · 2025 · PMID 40883986not yet assessed
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Five-year analysis of efficacy and safety of a bidirectional AAV gene therapy in Tay-Sachs sheep ↗Journal of Clinical Investigation · 2025 · PMID 41026525not yet assessed
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Lacticaseibacillus paracasei subsp. paracasei Q- 1 Exhibits Good Safety and Effectively Prevents Escherichia coli K99-Induced Diarrhea in Mice ↗Probiotics and Antimicrobial Proteins · 2025 · PMID 40295465not yet assessed
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The Immunogenicity of AAV-Encoded HIV-1 bNAbs in Rhesus Macaques Is Unaffected by a Short Course of the Immunomodulator CTLA4Ig ↗AIDS Research and Human Retroviruses · 2025 · PMID 40833809not yet assessed
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The 2024 Nobel Prize: Impact of the Discovery of miRNA on the Field of Gene Therapy ↗Human Gene Therapy · 2025 · PMID 39752182not yet assessed
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A single amino acid variant in the variable region I of AAV capsid confers liver detargeting ↗bioRxiv (Cold Spring Harbor Laboratory) · 2025 · PMID 40093067not yet assessed
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AAVone: A Cost-Effective, Single-Plasmid Solution for Efficient AAV Production with Reduced DNA Impurities ↗bioRxiv (Cold Spring Harbor Laboratory) · 2025 · PMID 39829756not yet assessed
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Behavioral Efficacy of AAV FOXG1 Gene Replacement Therapy in a Mouse Model of FOXG1 Syndrome ↗bioRxiv (Cold Spring Harbor Laboratory) · 2025not yet assessed
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Lactobacillus paracasei LCQ-1 Exhibits Good Safety and Effectively Prevents Escherichia coli K99-Induced Diarrhea in Mice ↗Research Square · 2025not yet assessed
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Drug resistance and pathogenicity characteristics of Escherichia coli causing pneumonia in farmed foxes ↗Frontiers in Veterinary Science · 2025 · PMID 40271487not yet assessed
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A Compact Base Editor Rescues AATD-associated Liver and Lung Disease in Mouse Models ↗bioRxiv (Cold Spring Harbor Laboratory) · 2025 · PMID 40654892not yet assessed
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Engineering novel AAV capsids by global de-targeting and subsequent muscle-specific tropism in mice and NHPs ↗Research Square · 2025not yet assessed
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Gene therapies alleviate absence epilepsy associated with Scn2a deficiency in DBA/2J mice ↗bioRxiv (Cold Spring Harbor Laboratory) · 2025 · PMID 40501831not yet assessed
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“Seipin mediates Perilipin-1 recruitment to lipid droplets to preserve human adipocyte identity” ↗bioRxiv (Cold Spring Harbor Laboratory) · 2025 · PMID 41292895not yet assessed
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Adeno-associated virus as a delivery vector for gene therapy of human diseases ↗Signal Transduction and Targeted Therapy · 2024 · PMID 38565561not yet assessed
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Recombinant adeno-associated virus as a delivery platform for ocular gene therapy: A comprehensive review ↗Molecular Therapy · 2024 · PMID 39489915not yet assessed
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Improved gene therapy for spinal muscular atrophy in mice using codon-optimized hSMN1 transgene and hSMN1 gene-derived promotor ↗EMBO Molecular Medicine · 2024 · PMID 38413838not yet assessed
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Potential limitations of microdystrophin gene therapy for Duchenne muscular dystrophy ↗JCI Insight · 2024 · PMID 38713520not yet assessed
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Oligonucleotide therapies for nonalcoholic steatohepatitis ↗Molecular Therapy — Nucleic Acids · 2024 · PMID 38665220not yet assessed
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The AAV2.7m8 capsid packages a higher degree of heterogeneous vector genomes than AAV2 ↗Gene Therapy · 2024 · PMID 39134629not yet assessed
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Domain-inlaid Nme2Cas9 adenine base editors with improved activity and targeting scope ↗Nature Communications · 2024 · PMID 38368418not yet assessed
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Development of AAV-Mediated Gene Therapy Approaches to Treat Skeletal Diseases ↗Human Gene Therapy · 2024 · PMID 38534217not yet assessed
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Producing high-quantity and high-quality recombinant adeno-associated virus by low-cis triple transfection ↗Molecular Therapy — Methods & Clinical Development · 2024 · PMID 38558570not yet assessed
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Developing AAV-delivered nonsense suppressor tRNAs for neurological disorders ↗Neurotherapeutics · 2024 · PMID 38959711not yet assessed
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Efficacy and Safety of Adeno-Associated Virus-Based Clinical Gene Therapy for Hemophilia: A Systematic Review and Meta-Analysis ↗Human Gene Therapy · 2024 · PMID 38185849not yet assessed
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AAV5 Delivery of CRISPR/Cas9 Mediates Genome Editing in the Lungs of Young Rhesus Monkeys ↗Human Gene Therapy · 2024 · PMID 38767512not yet assessed
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Systemic gene therapy corrects the neurological phenotype in a mouse model of NGLY1 deficiency ↗JCI Insight · 2024 · PMID 39137042not yet assessed
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Advances in Bone-Targeting Drug Delivery: Emerging Strategies Using Adeno-Associated Virus ↗Human Gene Therapy · 2024 · PMID 38661537not yet assessed
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In vivo evolution of env in SHIV-AD8EO-infected rhesus macaques after AAV-vectored delivery of eCD4-Ig ↗Molecular Therapy · 2024 · PMID 39673132not yet assessed
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Gene replacement therapies for inherited disorders of neurotransmission: Current progress in succinic semialdehyde dehydrogenase deficiency ↗Journal of Inherited Metabolic Disease · 2024 · PMID 38581234not yet assessed
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How long do the effects of gene therapy based on adeno-associated virus last? A plain language summary ↗Future Rare Diseases · 2024not yet assessed
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A Comprehensive Atlas of AAV Tropism in the Mouse ↗bioRxiv (Cold Spring Harbor Laboratory) · 2024 · PMID 39314496not yet assessed
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Adeno-associated viral delivery of Env-specific antibodies prevents SIV rebound after discontinuing antiretroviral therapy ↗bioRxiv (Cold Spring Harbor Laboratory) · 2024 · PMID 38895320not yet assessed
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Unveiling the critical pathways in AAV potency evaluation and future trends in gene therapy ↗Cell and Gene Therapy Insights · 2024not yet assessed
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6.1 – 00142 Durable Viral Load Remission in SHIV-infected Macaques after Vectored Delivery of Monoclonal Antibodies ↗Journal of Virus Eradication · 2024not yet assessed
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PP6.2 – 00140 Avoiding unwanted host immune responses toward AAV-delivered anti-HIV antibodies ↗Journal of Virus Eradication · 2024not yet assessed
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Combinatorial design of nanoparticles for pulmonary mRNA delivery and genome editing ↗Nature Biotechnology · 2023 · PMID 36997680not yet assessed
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Base editing rescue of spinal muscular atrophy in cells and in mice ↗Science · 2023 · PMID 36996170not yet assessed
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Divalent siRNAs are bioavailable in the lung and efficiently block SARS-CoV-2 infection ↗Proceedings of the National Academy of Sciences · 2023 · PMID 36893269not yet assessed
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Therapeutic inhibition of miR-155 attenuates liver fibrosis via STAT3 signaling ↗Molecular Therapy — Nucleic Acids · 2023 · PMID 37547286not yet assessed
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Schnurri-3 inhibition suppresses bone and joint damage in models of rheumatoid arthritis ↗Proceedings of the National Academy of Sciences · 2023 · PMID 37141171not yet assessed
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Adeno-associated virus-mediated gene therapy in a patient with Canavan disease using dual routes of administration and immune modulation ↗Molecular Therapy — Methods & Clinical Development · 2023 · PMID 37601414not yet assessed
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Durable contraception in the female domestic cat using viral-vectored delivery of a feline anti-Müllerian hormone transgene ↗Nature Communications · 2023 · PMID 37280258not yet assessed
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AAV-based gene editing of type 1 collagen mutation to treat osteogenesis imperfecta ↗Molecular Therapy — Nucleic Acids · 2023 · PMID 38261950not yet assessed
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AAV-Mediated Targeting of the Activin A-ACVR1R206H Signaling in Fibrodysplasia Ossificans Progressiva ↗Biomolecules · 2023 · PMID 37759764not yet assessed
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Self-delivering, chemically modified CRISPR RNAs for AAV co-delivery and genome editing in vivo ↗Nucleic Acids Research · 2023 · PMID 38033325not yet assessed
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A strategy for high antibody expression with low anti-drug antibodies using AAV9 vectors ↗Frontiers in Immunology · 2023 · PMID 37153616not yet assessed
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Non-canonical amino acid incorporation into AAV5 capsid enhances lung transduction in mice ↗Molecular Therapy — Methods & Clinical Development · 2023 · PMID 37886602not yet assessed
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C9orf72 poly(PR) aggregation in nucleus induces ALS/FTD-related neurodegeneration in cynomolgus monkeys ↗Neurobiology of Disease · 2023 · PMID 37328037not yet assessed
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Renewal of oligodendrocyte lineage reverses dysmyelination and CNS neurodegeneration through corrected N-acetylaspartate metabolism ↗Progress in Neurobiology · 2023 · PMID 37149081not yet assessed
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Querying Recombination Junctions of Replication-Competent Adeno-Associated Viruses in Gene Therapy Vector Preparations with Single Molecule, Real-Time Sequencing ↗Viruses · 2023 · PMID 37376529not yet assessed
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A Fluorescent Reporter Mouse for In Vivo Assessment of Genome Editing with Diverse Cas Nucleases and Prime Editors ↗The CRISPR Journal · 2023 · PMID 38108517not yet assessed
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Rescue of GM3 synthase deficiency by spatially controlled, rAAV-mediated ST3GAL5 delivery ↗JCI Insight · 2023 · PMID 37014712not yet assessed
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Self-delivering CRISPR RNAs for AAV Co-delivery and Genome Editing in vivo ↗bioRxiv (Cold Spring Harbor Laboratory) · 2023 · PMID 36993169not yet assessed
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Engineering Nme2Cas9 Adenine Base Editors with Improved Activity and Targeting Scope ↗bioRxiv (Cold Spring Harbor Laboratory) · 2023 · PMID 37131611not yet assessed
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NIIMBL’s viral vector program: A cross-gene therapy community collaboration to transform viral vector development and manufacturing ↗Molecular Therapy · 2023 · PMID 37989318not yet assessed
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Drag-and-drop genome insertion of large sequences without double-strand DNA cleavage using CRISPR-directed integrases ↗Nature Biotechnology · 2022 · PMID 36424489not yet assessed
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Evaluating the state of the science for adeno-associated virus integration: An integrated perspective ↗Molecular Therapy · 2022 · PMID 35690906not yet assessed
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AAV-delivered suppressor tRNA overcomes a nonsense mutation in mice ↗Nature · 2022 · PMID 35322228not yet assessed
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Durability of transgene expression after rAAV gene therapy ↗Molecular Therapy · 2022 · PMID 35283274not yet assessed
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WNT-modulating gene silencers as a gene therapy for osteoporosis, bone fracture, and critical-sized bone defects ↗Molecular Therapy · 2022 · PMID 36184851not yet assessed
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Human and Insect Cell-Produced Recombinant Adeno-Associated Viruses Show Differences in Genome Heterogeneity ↗Human Gene Therapy · 2022 · PMID 35293222not yet assessed
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Adenine Base Editing In Vivo with a Single Adeno-Associated Virus Vector ↗GEN Biotechnology · 2022 · PMID 35811581not yet assessed
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Graphene quantum dots rescue angiogenic retinopathy via blocking STAT3/Periostin/ERK signaling ↗Journal of Nanobiotechnology · 2022 · PMID 35366885not yet assessed
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Ocular Drug Delivery: Advancements and Innovations ↗Pharmaceutics · 2022 · PMID 36145679not yet assessed
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Impaired mitochondrial oxidative metabolism in skeletal progenitor cells leads to musculoskeletal disintegration ↗Nature Communications · 2022 · PMID 36369293not yet assessed
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Suppression of heterotopic ossification in fibrodysplasia ossificans progressiva using AAV gene delivery ↗Nature Communications · 2022 · PMID 36258013not yet assessed
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Direct ITR-to-ITR Nanopore Sequencing of AAV Vector Genomes ↗Human Gene Therapy · 2022 · PMID 36178359not yet assessed
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High concordance of ELISA and neutralization assays allows for the detection of antibodies to individual AAV serotypes ↗Molecular Therapy — Methods & Clinical Development · 2022 · PMID 35141348not yet assessed
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Paradoxical activation of transcription factor SREBP1c and de novo lipogenesis by hepatocyte-selective ATP-citrate lyase depletion in obese mice ↗Journal of Biological Chemistry · 2022 · PMID 35988648not yet assessed
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AAV-mediated delivery of osteoblast/osteoclast-regulating miRNAs for osteoporosis therapy ↗Molecular Therapy — Nucleic Acids · 2022 · PMID 35950212not yet assessed
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Gene-based therapeutics for rare genetic neurodevelopmental psychiatric disorders ↗Molecular Therapy · 2022 · PMID 35585789not yet assessed
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Regulation of sclerostin by the SIRT1 stabilization pathway in osteocytes ↗Cell Death and Differentiation · 2022 · PMID 35169297not yet assessed
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Phosphorylation of RXRα mediates the effect of JNK to suppress hepatic FGF21 expression and promote metabolic syndrome ↗Proceedings of the National Academy of Sciences · 2022 · PMID 36282921not yet assessed
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Gene Therapy for Fibrodysplasia Ossificans Progressiva: Feasibility and Obstacles ↗Human Gene Therapy · 2022 · PMID 35502479not yet assessed
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Exosomes Derived from Gold Nanorod Engineered Vascular Endothelial Cells Inhibit Tumor Growth via Disrupting the TGFβ Pathway ↗Journal of Nanomaterials · 2022not yet assessed
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Paradoxical activation of SREBP1c and de novo lipogenesis by hepatocyte-selective ACLY depletion in obese mice ↗bioRxiv (Cold Spring Harbor Laboratory) · 2022not yet assessed
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Suppression of Heterotopic Ossification in Fibrodysplasia Ossificans Progressiva Using AAV Gene Delivery ↗Research Square · 2022not yet assessed
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Potential limitations of micro-dystrophin gene therapy for Duchenne muscular dystrophy ↗bioRxiv (Cold Spring Harbor Laboratory) · 2022not yet assessed
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Reuben Matalon, MD, PhD, FACMG (1935–2021) ↗Human Gene Therapy · 2022not yet assessed
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An efficacious and safe rescue of GM3 synthase deficiency by spatially regulated rAAV-mediated ST3GAL5 delivery ↗Research Square · 2022not yet assessed
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Letter to the Editor: mRNA Vaccines in Urological Malignancies ↗Human Gene Therapy · 2022 · PMID 36282986not yet assessed
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Viral vector platforms within the gene therapy landscape ↗Signal Transduction and Targeted Therapy · 2021 · PMID 33558455not yet assessed
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Improved prime editors enable pathogenic allele correction and cancer modelling in adult mice ↗Nature Communications · 2021 · PMID 33837189not yet assessed
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Overcoming innate immune barriers that impede AAV gene therapy vectors ↗Journal of Clinical Investigation · 2021 · PMID 33393506not yet assessed
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Engineering adeno-associated viral vectors to evade innate immune and inflammatory responses ↗Science Translational Medicine · 2021 · PMID 33568518not yet assessed
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The NIH Somatic Cell Genome Editing program ↗Nature · 2021 · PMID 33828315not yet assessed
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Dynamics of a disinhibitory prefrontal microcircuit in controlling social competition ↗Neuron · 2021 · PMID 34793692not yet assessed
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Self-inactivating, all-in-one AAV vectors for precision Cas9 genome editing via homology-directed repair in vivo ↗Nature Communications · 2021 · PMID 34725353not yet assessed
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Single-cell sequencing reveals suppressive transcriptional programs regulated by MIS/AMH in neonatal ovaries ↗Proceedings of the National Academy of Sciences · 2021 · PMID 33980714not yet assessed
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Start codon disruption with CRISPR/Cas9 prevents murine Fuchs’ endothelial corneal dystrophy ↗eLife · 2021 · PMID 34100716not yet assessed
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Novel Combinatorial MicroRNA-Binding Sites in AAV Vectors Synergistically Diminish Antigen Presentation and Transgene Immunity for Efficient and Stable Transduction ↗Frontiers in Immunology · 2021 · PMID 33995418not yet assessed
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AAV5 delivery of CRISPR-Cas9 supports effective genome editing in mouse lung airway ↗Molecular Therapy · 2021 · PMID 34695545not yet assessed
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Modulating immune responses to AAV by expanded polyclonal T-regs and capsid specific chimeric antigen receptor T-regulatory cells ↗Molecular Therapy — Methods & Clinical Development · 2021 · PMID 34853797not yet assessed
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Vectored Immunotherapeutics for Infectious Diseases: Can rAAVs Be The Game Changers for Fighting Transmissible Pathogens? ↗Frontiers in Immunology · 2021 · PMID 34046041not yet assessed
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Synergistic Deoxynucleoside and Gene Therapies for Thymidine Kinase 2 Deficiency ↗Annals of Neurology · 2021 · PMID 34338329not yet assessed
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Efficacious, safe, and stable inhibition of corneal neovascularization by AAV-vectored anti-VEGF therapeutics ↗Molecular Therapy — Methods & Clinical Development · 2021 · PMID 34514023not yet assessed
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Cellular and Tissue Selectivity of AAV Serotypes for Gene Delivery to Chondrocytes and Cartilage ↗International Journal of Medical Sciences · 2021 · PMID 34522160not yet assessed
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Low-Dose Recombinant Adeno-Associated Virus-Mediated Inhibition of Vascular Endothelial Growth Factor Can Treat Neovascular Pathologies Without Inducing Retinal Vasculitis ↗Human Gene Therapy · 2021 · PMID 34182803not yet assessed
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Canavan Disease as a Model for Gene Therapy-Mediated Myelin Repair ↗Frontiers in Cellular Neuroscience · 2021 · PMID 33967698not yet assessed
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Next-generation strategies for gene-targeted therapies of central nervous system disorders: A workshop summary ↗Molecular Therapy · 2021 · PMID 34547463not yet assessed
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Coagulation factor IX gene transfer to non-human primates using engineered AAV3 capsid and hepatic optimized expression cassette ↗Molecular Therapy — Methods & Clinical Development · 2021 · PMID 34631930not yet assessed
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rAAV-delivered PTEN therapeutics for prostate cancer ↗Molecular Therapy — Nucleic Acids · 2021 · PMID 34976432not yet assessed
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Large-scale molecular epidemiological analysis of AAV in a cancer patient population ↗Oncogene · 2021 · PMID 33782545not yet assessed
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AAV-Mediated Gene Therapy for Glycosphingolipid Biosynthesis Deficiencies ↗Trends in Molecular Medicine · 2021 · PMID 33714697not yet assessed
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Membranous Bubbles: High-Purity and High-Titer Exosomes as the Potential Solution for Adeno-Associated Viruses to Evade Neutralization? ↗Human Gene Therapy · 2021 · PMID 34935455not yet assessed
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Oncolytic Virus Alphavirus M1: A New and Promising Weapon to Fight Cancer ↗Human Gene Therapy · 2021 · PMID 33621140not yet assessed
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rAAV-based and intraprostatically delivered miR-34a therapeutics for efficient inhibition of prostate cancer progression ↗Gene Therapy · 2021 · PMID 34226687not yet assessed
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Suprachoroidal Injections of AAV for Retinal Gene Delivery in mouseInvestigative Ophthalmology & Visual Science · 2021not yet assessed
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Editorial: “AAV Gene Therapy: Immunology and Immunotherapeutics” ↗Frontiers in Immunology · 2021 · PMID 34992614not yet assessed
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Immune Responses to Recombinant Adenoviruses As Gene Therapy Vectors and COVID-19 Vaccines: A Two-Edged Sword ↗Human Gene Therapy · 2021 · PMID 34283643not yet assessed
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Adenine Base Editing in vivo with a Single Adeno-Associated Virus Vector ↗bioRxiv (Cold Spring Harbor Laboratory) · 2021not yet assessed
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It Is Time to Call Anti-Asian Bias What It Is: Racism ↗Human Gene Therapy · 2021 · PMID 34003044not yet assessed
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not yet assessed
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Inhibition of corneal neovascularization with rAAV-anti-VEGF in mouse corneal injury modelsInvestigative Ophthalmology & Visual Science · 2021not yet assessed
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Low-dose rAAV-mediated inhibition of VEGF can treat neovascular pathologies without inducing retinal vasculitisInvestigative Ophthalmology & Visual Science · 2021not yet assessed
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Targeted Nanoparticle‐Mediated Gene Therapy Mimics Oncolytic Virus for Effective Melanoma Treatment ↗Advanced Functional Materials · 2021not yet assessed
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CRISPR-Based Therapeutic Genome Editing: Strategies and In Vivo Delivery by AAV Vectors ↗Cell · 2020 · PMID 32243786not yet assessed
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LATS suppresses mTORC1 activity to directly coordinate Hippo and mTORC1 pathways in growth control ↗Nature Cell Biology · 2020 · PMID 32015438not yet assessed
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AAV-Genome Population Sequencing of Vectors Packaging CRISPR Components Reveals Design-Influenced Heterogeneity ↗Molecular Therapy — Methods & Clinical Development · 2020 · PMID 32775498not yet assessed
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Structural characterization of a novel human adeno-associated virus capsid with neurotropic properties ↗Nature Communications · 2020 · PMID 32606306not yet assessed
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Long-Term Delivery of an Anti-SIV Monoclonal Antibody With AAV ↗Frontiers in Immunology · 2020 · PMID 32256496not yet assessed
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Bone-Targeting AAV-Mediated Gene Silencing in Osteoclasts for Osteoporosis Therapy ↗Molecular Therapy — Methods & Clinical Development · 2020 · PMID 32405514not yet assessed
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Two-Plasmid Packaging System for Recombinant Adeno-Associated Virus ↗BioResearch open access · 2020 · PMID 33117614not yet assessed
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Is smaller better? Vaccine targeting recombinant receptor-binding domain might hold the key for mass production of effective prophylactics to fight the COVID-19 pandemic ↗Signal Transduction and Targeted Therapy · 2020 · PMID 33024086not yet assessed
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Glycoengineering of AAV-delivered monoclonal antibodies yields increased ADCC activity ↗Molecular Therapy — Methods & Clinical Development · 2020 · PMID 33426147not yet assessed
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2020: Gene Therapy Enters Its Fourth Decade ↗Human Gene Therapy · 2020 · PMID 31967921not yet assessed
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High dose systemic gene therapy: emerging trends on safety and efficacy ↗Cell and Gene Therapy Insights · 2020not yet assessed
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Introducing Genes into Mammalian Cells: Viral Vectors ↗Cold Spring Harbor Protocols · 2020 · PMID 32457039not yet assessed
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Improved prime editors enable pathogenic allele correction and cancer modelling in adult mice ↗bioRxiv (Cold Spring Harbor Laboratory) · 2020not yet assessed
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A feed-forward regulatory loop in adipose tissue promotes signaling by the hepatokine FGF21 ↗Genes & Development · 2020 · PMID 33334822not yet assessed
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Production of Recombinant Adeno-Associated Viruses (rAAVs) by Transient Transfection ↗Cold Spring Harbor Protocols · 2020 · PMID 32015001not yet assessed
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Purification of Recombinant Adeno-Associated Viruses (rAAVs) by Cesium Chloride Gradient Sedimentation ↗Cold Spring Harbor Protocols · 2020 · PMID 32747580not yet assessed
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Analysis of Recombinant Adeno-Associated Virus (rAAV) Purity Using Silver-Stained SDS-PAGE ↗Cold Spring Harbor Protocols · 2020 · PMID 32747582not yet assessed
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Titration of Recombinant Adeno-Associated Virus (rAAV) Genome Copy Number Using Real-Time Quantitative Polymerase Chain Reaction (qPCR) ↗Cold Spring Harbor Protocols · 2020 · PMID 32358049not yet assessed
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Analysis of Recombinant Adeno-Associated Virus (rAAV) Sample Morphology Using Negative Staining and High-Resolution Electron Microscopy ↗Cold Spring Harbor Protocols · 2020 · PMID 32747581not yet assessed
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Sensitive Determination of Infectious Titer of Recombinant Adeno-Associated Viruses (rAAVs) Using TCID50 End-Point Dilution and Quantitative Polymerase Chain Reaction (qPCR) ↗Cold Spring Harbor Protocols · 2020 · PMID 32358050not yet assessed
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Purification of Recombinant Adeno-Associated Viruses (rAAVs) by Iodixanol Gradient Centrifugation ↗Cold Spring Harbor Protocols · 2020 · PMID 32015002not yet assessed
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Purification of Recombinant Adeno-Associated Virus 2 (rAAV2) by Heparin Column Affinity Chromatography ↗Cold Spring Harbor Protocols · 2020 · PMID 32358048not yet assessed
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Start codon disruption with CRISPR/Cas9 prevents murine Fuchs’ endothelial corneal dystrophy ↗bioRxiv (Cold Spring Harbor Laboratory) · 2020not yet assessed
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Enrichment of Fully Packaged Virions in Column-Purified Recombinant Adeno-Associated Virus (rAAV) Preparations by Iodixanol Gradient Centrifugation Followed by Anion-Exchange Column Chromatography ↗Cold Spring Harbor Protocols · 2020 · PMID 32015003not yet assessed
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Precision Cas9 Genome Editing in vivo with All-in-one, Self-targeting AAV Vectors ↗bioRxiv (Cold Spring Harbor Laboratory) · 2020not yet assessed
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Voyager Therapeutics - A Spinout from UMass Gene Therapy and RNAi Technologies ↗eScholarship@UMassChan · 2020not yet assessed
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Ringing in the Changes ↗Human Gene Therapy · 2020 · PMID 31967918not yet assessed
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Synergistic effect of deoxynucleosides and AAV gene therapy for thymidine kinase 2 deficiency ↗bioRxiv (Cold Spring Harbor Laboratory) · 2020not yet assessed
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rAAV-Delivered PTEN Therapeutics for Prostate Cancer ↗Research Square · 2020not yet assessed
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CNS-restricted Transduction and CRISPR/Cas9-mediated Gene Deletion with an Engineered AAV Vector ↗Carolina Digital Repository (University of North Carolina at Chapel Hill) · 2020not yet assessed
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Adeno-Associated Virus Type 2 and Hepatocellular Carcinoma? ↗Carolina Digital Repository (University of North Carolina at Chapel Hill) · 2020not yet assessed
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Adeno-associated virus vector as a platform for gene therapy delivery ↗Nature Reviews Drug Discovery · 2019 · PMID 30710128not yet assessed
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Targeted Complement Inhibition at Synapses Prevents Microglial Synaptic Engulfment and Synapse Loss in Demyelinating Disease ↗Immunity · 2019 · PMID 31883839not yet assessed
-
Bone-targeting AAV-mediated silencing of Schnurri-3 prevents bone loss in osteoporosis ↗Nature Communications · 2019 · PMID 31273195not yet assessed
-
Adeno-Associated Virus Delivery of Anti-HIV Monoclonal Antibodies Can Drive Long-Term Virologic Suppression ↗Immunity · 2019 · PMID 30850342not yet assessed
-
Curing hemophilia A by NHEJ-mediated ectopic F8 insertion in the mouse ↗Genome biology · 2019 · PMID 31843008not yet assessed
-
Quantitative and Digital Droplet-Based AAV Genome Titration ↗Methods in molecular biology · 2019 · PMID 30783968not yet assessed
-
Fetal Gene Therapy Using a Single Injection of Recombinant AAV9 Rescued SMA Phenotype in Mice ↗Molecular Therapy · 2019 · PMID 31543414not yet assessed
-
Single-cell sequencing of neonatal uterus reveals an Misr2+ endometrial progenitor indispensable for fertility ↗eLife · 2019 · PMID 31232694not yet assessed
-
Circumventing cellular immunity by miR142-mediated regulation sufficiently supports rAAV-delivered OVA expression without activating humoral immunity ↗JCI Insight · 2019 · PMID 31112525not yet assessed
-
Inhibition of miR-378a-3p by Inflammation Enhances IL-33 Levels: A Novel Mechanism of Alarmin Modulation in Ulcerative Colitis ↗Frontiers in Immunology · 2019 · PMID 31824476not yet assessed
-
Comparative Analysis of the Capsid Structures of AAVrh.10, AAVrh.39, and AAV8 ↗Journal of Virology · 2019 · PMID 31826994not yet assessed
-
Anti-drug Antibody Responses Impair Prophylaxis Mediated by AAV-Delivered HIV-1 Broadly Neutralizing Antibodies ↗Molecular Therapy · 2019 · PMID 30704961not yet assessed
-
AAV-delivered eCD4-Ig protects rhesus macaques from high-dose SIVmac239 challenges ↗Science Translational Medicine · 2019 · PMID 31341061not yet assessed
-
Intravenous Infusion of AAV for Widespread Gene Delivery to the Nervous System ↗Methods in molecular biology · 2019 · PMID 30783972not yet assessed
-
Effective and Accurate Gene Silencing by a Recombinant AAV-Compatible MicroRNA Scaffold ↗Molecular Therapy · 2019 · PMID 31843447not yet assessed
-
Conditional, inducible gene silencing in dopamine neurons reveals a sex-specific role for Rit2 GTPase in acute cocaine response and striatal function ↗Neuropsychopharmacology · 2019 · PMID 31277075not yet assessed
-
Liver-Directed but Not Muscle-Directed AAV-Antibody Gene Transfer Limits Humoral Immune Responses in Rhesus Monkeys ↗Molecular Therapy — Methods & Clinical Development · 2019 · PMID 31890736not yet assessed
-
Evaluation of portable colposcopy and human papillomavirus testing for screening of cervical cancer in rural China ↗International Journal of Gynecological Cancer · 2019 · PMID 30640679not yet assessed
-
Evaluation of portable colposcopy and HPV testing for screening of cervical cancer in rural China ↗Gynecologic Oncology · 2019not yet assessed
-
High-Throughput Quantification of In Vivo Adeno-Associated Virus Transduction with Barcoded Non-Coding RNAs ↗Human Gene Therapy · 2019 · PMID 31072208not yet assessed
-
Gene Delivery to Nonhuman Primate Preimplantation Embryos Using Recombinant Adeno‐Associated Virus ↗Advanced Science · 2019 · PMID 31728271not yet assessed
-
not yet assessed
-
Targeted complement inhibition at synapses prevents microglial synaptic engulfment and synapse loss in demyelinating disease ↗bioRxiv (Cold Spring Harbor Laboratory) · 2019not yet assessed
-
Measuring the Infectious Titer of Recombinant Adenovirus Using Tissue Culture Infection Dose 50% (TCID50) End-Point Dilution and Quantitative Polymerase Chain Reaction (qPCR) ↗Cold Spring Harbor Protocols · 2019 · PMID 31371467not yet assessed
-
Purification of the Recombinant Adenovirus by Cesium Chloride Gradient Centrifugation ↗Cold Spring Harbor Protocols · 2019 · PMID 31043560not yet assessed
-
Release of the Cloned Recombinant Adenovirus Genome for Rescue and Expansion ↗Cold Spring Harbor Protocols · 2019 · PMID 31043559not yet assessed
-
Prime Editing: A Novel Cas9-Reverse Transcriptase Fusion May Revolutionize Genome Editing ↗Human Gene Therapy · 2019 · PMID 31860398not yet assessed
-
Construction of Recombinant Adenovirus Genomes by Direct Cloning ↗Cold Spring Harbor Protocols · 2019 · PMID 31043558not yet assessed
-
Preparation of a DNA Standard for Quantitative Polymerase Chain Reaction (qPCR) ↗Cold Spring Harbor Protocols · 2019 · PMID 31371468not yet assessed
-
Detection Assay for Replication-Competent Adenovirus by Concentration Passage and Real-Time Quantitative Polymerase Chain Reaction (qPCR) ↗Cold Spring Harbor Protocols · 2019 · PMID 31792138not yet assessed
-
Conditional, inducible gene silencing in dopamine neurons reveals a sex-specific role for Rit2 GTPase in acute cocaine response and striatal function ↗bioRxiv (Cold Spring Harbor Laboratory) · 2019not yet assessed
-
Characterization of the Purified Recombinant Adenovirus for Viral Genome Structure by Restriction Enzyme Digestions ↗Cold Spring Harbor Protocols · 2019 · PMID 31792137not yet assessed
-
not yet assessed
-
Detection of virulence and resistance gene and drug sensitivity analysis of Escherichia coli in fur-bearing animal.Zhongguo yufang shouyi xuebao · 2019not yet assessed
-
Adeno-associated Virus Genome Population Sequencing Achieves Full Vector Genome Resolution and Reveals Human-Vector Chimeras ↗Molecular Therapy — Methods & Clinical Development · 2018 · PMID 29766023not yet assessed
-
Streamlined ex vivo and in vivo genome editing in mouse embryos using recombinant adeno-associated viruses ↗Nature Communications · 2018 · PMID 29379011not yet assessed
-
A Rationally Engineered Capsid Variant of AAV9 for Systemic CNS-Directed and Peripheral Tissue-Detargeted Gene Delivery in Neonates ↗Molecular Therapy — Methods & Clinical Development · 2018 · PMID 29766031not yet assessed
-
In Vivo Genome Editing Partially Restores Alpha1-Antitrypsin in a Murine Model of AAT Deficiency ↗Human Gene Therapy · 2018 · PMID 29597895not yet assessed
-
Adeno-Associated Virus Neutralizing Antibodies in Large Animals and Their Impact on Brain Intraparenchymal Gene Transfer ↗Molecular Therapy — Methods & Clinical Development · 2018 · PMID 30397628not yet assessed
-
Down-regulation of microRNA-203-3p initiates type 2 pathology during schistosome infection via elevation of interleukin-33 ↗PLoS Pathogens · 2018 · PMID 29554131not yet assessed
-
Intrathecal Adeno-Associated Viral Vector-Mediated Gene Delivery for Adrenomyeloneuropathy ↗Human Gene Therapy · 2018 · PMID 30358470not yet assessed
-
Cas9-mediated allelic exchange repairs compound heterozygous recessive mutations in mice ↗Nature Biotechnology · 2018 · PMID 30102296not yet assessed
-
Clinical Evaluations of Toxicity and Efficacy of Nanoparticle-Mediated Gene Therapy ↗Human Gene Therapy · 2018 · PMID 29893153not yet assessed
-
MicroRNA-96 Promotes Schistosomiasis Hepatic Fibrosis in Mice by Suppressing Smad7 ↗Molecular Therapy — Methods & Clinical Development · 2018 · PMID 30406154not yet assessed
-
Targeted Nanoparticle‐Mediated Gene Therapy Mimics Oncolytic Virus for Effective Melanoma Treatment ↗Advanced Functional Materials · 2018not yet assessed
-
Impact of neutralizing antibodies against AAV is a key consideration in gene transfer to nonhuman primates ↗Nature Medicine · 2018 · PMID 29867233not yet assessed
-
Selective Neuronal Uptake and Distribution of AAVrh8, AAV9, and AAVrh10 in Sheep After Intra-Striatal Administration ↗Journal of Huntington s Disease · 2018 · PMID 30320596not yet assessed
-
Cancer Therapy: Targeted Nanoparticle‐Mediated Gene Therapy Mimics Oncolytic Virus for Effective Melanoma Treatment (Adv. Funct. Mater. 29/2018) ↗Advanced Functional Materials · 2018not yet assessed
-
Slow Infusion of Recombinant Adeno-Associated Viruses into the Mouse Cerebrospinal Fluid Space ↗Human Gene Therapy Methods · 2018 · PMID 29596011not yet assessed
-
Taking a Hint from Structural Biology: To Better Understand AAV Transport across the BBB ↗Molecular Therapy · 2018 · PMID 29398483not yet assessed
-
Titration of Lentivirus Vectors ↗Cold Spring Harbor Protocols · 2018 · PMID 29610363not yet assessed
-
Production of High-Titer Retrovirus and Lentivirus Vectors ↗Cold Spring Harbor Protocols · 2018 · PMID 29610362not yet assessed
-
Monitoring Lentivirus Vector Stocks for Replication-Competent Viruses ↗Cold Spring Harbor Protocols · 2018 · PMID 29610364not yet assessed
-
Gene and Cell Therapy in China: Highlighting Excellence in the 21st Century 中国的基因与细胞治疗: 21世纪的飞跃发展和重要贡献 ↗Human Gene Therapy · 2018 · PMID 29446999not yet assessed
-
rAAV-based and intraprostatically delivered miR-34a therapeutics for efficient inhibition of prostate cancer progression ↗European Urology Supplements · 2018not yet assessed
-
Therapeutic efficacy of AAV-mediated factor H gene transfer in a murine model of lethal C3 glomerulopathy ↗Molecular Immunology · 2018not yet assessed
-
Regulation of RIPK1 activation by TAK1-mediated phosphorylation dictates apoptosis and necroptosis ↗Nature Communications · 2017 · PMID 28842570not yet assessed
-
AMH/MIS as a contraceptive that protects the ovarian reserve during chemotherapy ↗Proceedings of the National Academy of Sciences · 2017 · PMID 28137855not yet assessed
-
MicroRNA 122, Regulated by GRLH2, Protects Livers of Mice and Patients From Ethanol-Induced Liver Disease ↗Gastroenterology · 2017 · PMID 28987423not yet assessed
-
Brain microvasculature defects and Glut1 deficiency syndrome averted by early repletion of the glucose transporter-1 protein ↗Nature Communications · 2017 · PMID 28106060not yet assessed
-
Short DNA Hairpins Compromise Recombinant Adeno-Associated Virus Genome Homogeneity ↗Molecular Therapy · 2017 · PMID 28462820not yet assessed
-
Artificial miRNAs Reduce Human Mutant Huntingtin Throughout the Striatum in a Transgenic Sheep Model of Huntington's Disease ↗Human Gene Therapy · 2017 · PMID 29207890not yet assessed
-
Delivery of Adeno-Associated Virus Vectors in Adult Mammalian Inner-Ear Cell Subtypes Without Auditory Dysfunction ↗Human Gene Therapy · 2017 · PMID 29130354not yet assessed
-
Fat mass and obesity-associated protein attenuates lipid accumulation in macrophage foam cells and alleviates atherosclerosis in apolipoprotein E-deficient mice ↗Journal of Hypertension · 2017 · PMID 28253220not yet assessed
-
Redirecting N-acetylaspartate metabolism in the central nervous system normalizes myelination and rescues Canavan disease ↗JCI Insight · 2017 · PMID 28194442not yet assessed
-
Gene Therapy Using a miniCEP290 Fragment Delays Photoreceptor Degeneration in a Mouse Model of Leber Congenital Amaurosis ↗Human Gene Therapy · 2017 · PMID 28679290not yet assessed
-
Intracranial AAV ‐ IFN ‐β gene therapy eliminates invasive xenograft glioblastoma and improves survival in orthotopic syngeneic murine model ↗Molecular Oncology · 2017 · PMID 28098415not yet assessed
-
Transcriptome Profiling of Neovascularized Corneas Reveals miR-204 as a Multi-target Biotherapy Deliverable by rAAVs ↗Molecular Therapy — Nucleic Acids · 2017 · PMID 29499946not yet assessed
-
Adeno-associated virus serotype rh.10 displays strong muscle tropism following intraperitoneal delivery ↗Scientific Reports · 2017 · PMID 28067312not yet assessed
-
A Scalable and Accurate Method for Quantifying Vector Genomes of Recombinant Adeno-Associated Viruses in Crude Lysate ↗Human Gene Therapy Methods · 2017 · PMID 28488944not yet assessed
-
A Preclinical Study in Rhesus Macaques for Cystic Fibrosis to Assess Gene Transfer and Transduction by AAV1 and AAV5 with a Dual-Luciferase Reporter System ↗Human Gene Therapy Clinical Development · 2017 · PMID 28726496not yet assessed
-
Rod Outer Segment Development Influences AAV-Mediated Photoreceptor Transduction After Subretinal Injection ↗Human Gene Therapy · 2017 · PMID 28510482not yet assessed
-
Slow Intrathecal Injection of rAAVrh10 Enhances its Transduction of Spinal Cord and Therapeutic Efficacy in a Mutant SOD1 Model of ALS ↗Neuroscience · 2017 · PMID 29024785not yet assessed
-
Dengue Virus Evades AAV-Mediated Neutralizing Antibody Prophylaxis in Rhesus Monkeys ↗Molecular Therapy · 2017 · PMID 28750738not yet assessed
-
The Sodium Channel β4 Auxiliary Subunit Selectively Controls Long-Term Depression in Core Nucleus Accumbens Medium Spiny Neurons ↗Frontiers in Cellular Neuroscience · 2017 · PMID 28243192not yet assessed
-
Nanoparticles co-delivering pVSVMP and pIL12 for synergistic gene therapy of colon cancer ↗RSC Advances · 2017not yet assessed
-
Characterization of adenoviral transduction profile in prostate cancer cells and normal prostate tissue ↗The Prostate · 2017 · PMID 28726259not yet assessed
-
AAV Is Now a Medicine: We Had Better Get This Right ↗Human Gene Therapy · 2017 · PMID 28414552not yet assessed
-
Human gene therapy - The road to today and beyond ↗Journal of Molecular and Genetic Medicine · 2017not yet assessed
-
Rod outer segments influence the efficiency of AAV-mediated rod transductionInvestigative Ophthalmology & Visual Science · 2017not yet assessed
-
not yet assessed
-
Therapeutic genome editing by combined viral and non-viral delivery of CRISPR system components in vivo ↗Nature Biotechnology · 2016 · PMID 26829318not yet assessed
-
Rational design of aptazyme riboswitches for efficient control of gene expression in mammalian cells ↗eLife · 2016 · PMID 27805569not yet assessed
-
Identification of Adeno-Associated Viral Vectors That Target Neonatal and Adult Mammalian Inner Ear Cell Subtypes ↗Human Gene Therapy · 2016 · PMID 27342665not yet assessed
-
MARCH1 regulates insulin sensitivity by controlling cell surface insulin receptor levels ↗Nature Communications · 2016 · PMID 27577745not yet assessed
-
Naturally Existing Oncolytic Virus M1 Is Nonpathogenic for the Nonhuman Primates After Multiple Rounds of Repeated Intravenous Injections ↗Human Gene Therapy · 2016 · PMID 27296553not yet assessed
-
CNS-restricted Transduction and CRISPR/Cas9-mediated Gene Deletion with an Engineered AAV Vector ↗Molecular Therapy — Nucleic Acids · 2016 · PMID 27434683not yet assessed
-
Small Intestine but Not Liver Lysophosphatidylcholine Acyltransferase 3 (Lpcat3) Deficiency Has a Dominant Effect on Plasma Lipid Metabolism ↗Journal of Biological Chemistry · 2016 · PMID 26828064not yet assessed
-
Systemic AAV9-IFNβ gene delivery treats highly invasive glioblastoma ↗Neuro-Oncology · 2016 · PMID 27194146not yet assessed
-
rAAV Gene Therapy in a Canavan's Disease Mouse Model Reveals Immune Impairments and an Extended Pathology Beyond the Central Nervous System ↗Molecular Therapy · 2016 · PMID 27039844not yet assessed
-
Recombinant AAV Vectors for Enhanced Expression of Authentic IgG ↗PLoS ONE · 2016 · PMID 27332822not yet assessed
-
Recombinant Adeno-Associated Virus Serotype 6 (rAAV6) Potently and Preferentially Transduces Rat Astrocytes In vitro and In vivo ↗Frontiers in Cellular Neuroscience · 2016 · PMID 27891076not yet assessed
-
RNA activation of haploinsufficient Foxg1 gene in murine neocortex ↗Scientific Reports · 2016 · PMID 27995975not yet assessed
-
Efficient Transduction of Corneal Stroma by Adeno-Associated Viral Serotype Vectors for Implications in Gene Therapy of Corneal Diseases ↗Human Gene Therapy · 2016 · PMID 27001051not yet assessed
-
7. High-Throughput Sequencing of AAV Proviral Libraries from the Human Population Reveals Novel Variants with Unprecedented Intra-and Inter-Tissue Diversity ↗Molecular Therapy · 2016not yet assessed
-
669. rAAV-Based and Intraprostatically Delivered miR-34a Therapeutics for Efficient Inhibition of Prostate Cancer Progression ↗Molecular Therapy · 2016not yet assessed
-
9. rAAV Designs Harboring DNA Secondary Structures with High Thermal Stabilities Produce Heterogenic Viral Genome Populations ↗Molecular Therapy · 2016not yet assessed
-
58. Pushing the Limits for Canavan Gene Therapy into Adulthood: Is There an Age Limit for Gene Therapy in CNS Disorders? ↗Molecular Therapy · 2016not yet assessed
-
Urinary glycosaminoglycan concentration as a biomarker for effectiveness of enzyme replacement and gene therapy in large animal models of mucopolysaccharidoses ↗Molecular Genetics and Metabolism · 2016not yet assessed
-
655 Grainyhead-Like 2, a Novel Hepatic Transcription Factor, Promotes Alcohol-induced Liver Injury, Steatosis and Inflammation via miR-122 Down-regulation ↗Gastroenterology · 2016not yet assessed
-
366. Hitting Two Birds with One Stone: How Efficacious Pre-Clinical Gene Therapy Cures Canavan Disease and Sheds Light onto the Pathomechanism ↗Molecular Therapy · 2016not yet assessed
-
290. A High-Throughput, Sensitive, Accurate and Reproducible Method for Quantifying Vector Genomes of Recombinant Adeno-Associated Viruses in Crude Lysate ↗Molecular Therapy · 2016not yet assessed
-
351. Efficacious Non-Oligodendrocyte Gene Therapy Suggests a New Dogma About CNS Compartmentalization of NAA Metabolism and Supports a Metabolic Sink Theory ↗Molecular Therapy · 2016not yet assessed
-
157. High-Field In Vivo Neuroimaging to Determine CNS Gene Therapy Outcome and Probe Disease Pathomechanism ↗Molecular Therapy · 2016not yet assessed
-
81. Downregulation of Immune Responsive Chemokines Are Associated AAV8-Mediated Transgene Immune Tolerance ↗Molecular Therapy · 2016not yet assessed
-
739. rAAV Delivered MicroRNA Therapeutics Towards Efficacious Treatment of Corneal Neovascularization ↗Molecular Therapy · 2016not yet assessed
-
90. Vector Biodistribution After Recombinant AAVrh10 Intrathecal Delivery in Non-Human Primates ↗Molecular Therapy · 2016not yet assessed
-
349. The Cure of Canavan Disease: Is It a Scientific Fiction or Clinical Reality? ↗Molecular Therapy · 2016not yet assessed
-
295. Intrathecal Delivery of rAAV9-ABCD1 by Osmotic Pump in a Mouse Model of Adrenomyeloneuropathy ↗Molecular Therapy · 2016not yet assessed
-
733. Somatically Repairing Compound Heterozygous Recessive Mutations by Chromosomal Cut-and-Paste for In Vivo Gene Therapy ↗Molecular Therapy · 2016not yet assessed
-
570. Transient Reconstitution of Cas9 Protein for Safer Gene Editing In Vivo - A Ferry Tale Starring rAAV Capsid ↗Molecular Therapy · 2016not yet assessed
-
ティラピアの病原性分離株の同定とその漢方薬感受性試験【JST・京大機械翻訳】He'nan nongye kexue · 2016not yet assessed
-
カラアカシタビラメ(CYNOGLOSSUS SEMILAEVIS皮膚潰瘍の病原体同定と薬物感受性分析を分離する【JST・京大機械翻訳】Zhongguo shouyi xuebao · 2016not yet assessed
-
not yet assessed
-
Isolation, identification of pathogenic bacteria of rotten skin disease in Tilapia mossambica and sensitivity test to Chinese herbal medicine.He'nan nongye kexue · 2016not yet assessed
-
Isolation and identification of pathogen of skin ulcer from cynoglossussemilaevis and analysis of antibiotic sensitivity.Zhongguo shouyi xuebao · 2016not yet assessed
-
Adenovirus-Mediated Somatic Genome Editing of Pten by CRISPR/Cas9 in Mouse Liver in Spite of Cas9-Specific Immune Responses ↗Human Gene Therapy · 2015 · PMID 26086867not yet assessed
-
AAV-expressed eCD4-Ig provides durable protection from multiple SHIV challenges ↗Nature · 2015 · PMID 25707797not yet assessed
-
Challenges in CRISPR/CAS9 Delivery: Potential Roles of Nonviral Vectors ↗Human Gene Therapy · 2015 · PMID 26176432not yet assessed
-
Increased CRF signalling in a ventral tegmental area-interpeduncular nucleus-medial habenula circuit induces anxiety during nicotine withdrawal ↗Nature Communications · 2015 · PMID 25898242not yet assessed
-
Widespread Central Nervous System Gene Transfer and Silencing After Systemic Delivery of Novel AAV-AS Vector ↗Molecular Therapy · 2015 · PMID 26708003not yet assessed
-
AAV-Delivered Antibody Mediates Significant Protective Effects against SIVmac239 Challenge in the Absence of Neutralizing Activity ↗PLoS Pathogens · 2015 · PMID 26248318not yet assessed
-
Evaluation of AAV-mediated Gene Therapy for Central Nervous System Disease in Canine Mucopolysaccharidosis VII ↗Molecular Therapy · 2015 · PMID 26447927not yet assessed
-
State-of-the-art human gene therapy: part I. Gene delivery technologies. ↗PubMed · 2015 · PMID 25091489not yet assessed
-
Systemic AAV9 gene transfer in adult GM1 gangliosidosis mice reduces lysosomal storage in CNS and extends lifespan ↗Human Molecular Genetics · 2015 · PMID 25964428not yet assessed
-
Host Anti-antibody Responses Following Adeno-associated Virus–mediated Delivery of Antibodies Against HIV and SIV in Rhesus Monkeys ↗Molecular Therapy · 2015 · PMID 26444083not yet assessed
-
Efficient and Targeted Transduction of Nonhuman Primate Liver With Systemically Delivered Optimized AAV3B Vectors ↗Molecular Therapy · 2015 · PMID 26403887not yet assessed
-
Intravitreal AAV2.COMP-Ang1 Prevents Neurovascular Degeneration in a Murine Model of Diabetic Retinopathy ↗Diabetes · 2015 · PMID 26340930not yet assessed
-
AAV9 delivering a modified human Mullerian inhibiting substance as a gene therapy in patient-derived xenografts of ovarian cancer ↗Proceedings of the National Academy of Sciences · 2015 · PMID 26216943not yet assessed
-
Stability and Compatibility of Recombinant Adeno-Associated Virus Under Conditions Commonly Encountered in Human Gene Therapy Trials ↗Human Gene Therapy Methods · 2015 · PMID 25819833not yet assessed
-
Novel Roles of GATA4/6 in the Postnatal Heart Identified through Temporally Controlled, Cardiomyocyte-Specific Gene Inactivation by Adeno-Associated Virus Delivery of Cre Recombinase ↗PLoS ONE · 2015 · PMID 26023924not yet assessed
-
Activation of Cyclic Adenosine Monophosphate Pathway Increases the Sensitivity of Cancer Cells to the Oncolytic Virus M1 ↗Molecular Therapy · 2015 · PMID 26373347not yet assessed
-
Cutting Edge: DNA in the Lung Microenvironment during Influenza Virus Infection Tempers Inflammation by Engaging the DNA Sensor AIM2 ↗The Journal of Immunology · 2015 · PMID 26590313not yet assessed
-
Adeno-Associated Virus-Mediated MicroRNA Delivery and Therapeutics ↗Seminars in Liver Disease · 2015 · PMID 25632938not yet assessed
-
Functional Upregulation of α4* Nicotinic Acetylcholine Receptors in VTA GABAergic Neurons Increases Sensitivity to Nicotine Reward ↗Journal of Neuroscience · 2015 · PMID 26041923not yet assessed
-
A Single Injection of Recombinant Adeno-Associated Virus into the Lumbar Cistern Delivers Transgene Expression Throughout the Whole Spinal Cord ↗Molecular Neurobiology · 2015 · PMID 26050084not yet assessed
-
Adenovirus-Mediated Somatic Genome Editing of Pten by CRISPR/Cas9 in Mouse Liver in Spite of Cas9-Specific Immune ResponsesDSpace@MIT (Massachusetts Institute of Technology) · 2015not yet assessed
-
Gene Therapy for the Treatment of Neurological Disorders: Metabolic Disorders ↗Methods in molecular biology · 2015 · PMID 26611604not yet assessed
-
Large-Scale Production of Adeno-Associated Viral Vector Serotype-9 Carrying the Human Survival Motor Neuron Gene ↗Molecular Biotechnology · 2015 · PMID 26607476not yet assessed
-
Adeno-associated Virus Serotype Vectors Efficiently Transduce Normal Prostate Tissue and Prostate Cancer Cells ↗European Urology · 2015 · PMID 26526960not yet assessed
-
14. Next Generation AAV Vectors for Limiting Systemic Leakage and Improving Safety Following CNS Administration ↗Molecular Therapy · 2015not yet assessed
-
502. Optimization of Intrathecal Delivery of AAV for Targeting the Spinal Compartment ↗Molecular Therapy · 2015not yet assessed
-
Correction: Corrigendum: Increased CRF signalling in a ventral tegmental area-interpeduncular nucleus-medial habenula circuit induces anxiety during nicotine withdrawal ↗Nature Communications · 2015not yet assessed
-
Abstract AS25: An adeno-associated virus (AAV) 9 vector delivering modified human mullerian inhibiting substance (MIS) as a gene therapy for ovarian cancer ↗Clinical Cancer Research · 2015not yet assessed
-
86. Comparison of CNS Transduction by Different AAV Capsids in Mouse and Non-Human Primate ↗Molecular Therapy · 2015not yet assessed
-
676. DNA Sequences Encoding shRNAs Can Replace Mutant ITR in scAAV Genome for Efficient Replication and Packaging and Transcribe shRNAs by pol III Promoter Activity of wt ITR for Efficient Gene Silencing ↗Molecular Therapy · 2015not yet assessed
-
457. Both Regulatory T and B Cells May Play Roles in Systemic Immune Tolerance Induced by rAAV-Mediated Gene Transfer to Liver ↗Molecular Therapy · 2015not yet assessed
-
496. From Gene Therapy to Gene Enhancement: Optimized Pre-Clinical Gene Therapy Transforms Mice with the Severest Canavan Disease Phenotype Into “Supermice” ↗Molecular Therapy · 2015not yet assessed
-
586. Development of Anti-Angiogenic miRNA Therapeutics for Corneal Neovascularization ↗Molecular Therapy · 2015not yet assessed
-
92. Detection and Characterization of Immune Response Against AAVrh10 Vector After Intrathecal Vector Delivery in Non-Human Primates ↗Molecular Therapy · 2015not yet assessed
-
Global CNS Transduction of Adult Mice by Intravenously Delivered rAAVrh.8 and rAAVrh.10 and Nonhuman Primates by rAAVrh.10 ↗Molecular Therapy · 2014 · PMID 24781136not yet assessed
-
The PPARα-FGF21 Hormone Axis Contributes to Metabolic Regulation by the Hepatic JNK Signaling Pathway ↗Cell Metabolism · 2014 · PMID 25043817not yet assessed
-
Empty virions in AAV8 vector preparations reduce transduction efficiency and may cause total viral particle dose-limiting side effects ↗Molecular Therapy — Methods & Clinical Development · 2014 · PMID 25485285not yet assessed
-
State-of-the-art human gene therapy: part II. Gene therapy strategies and clinical applications. ↗PubMed · 2014 · PMID 25227756not yet assessed
-
The potential of adeno-associated viral vectors for gene delivery to muscle tissue ↗Expert Opinion on Drug Delivery · 2014 · PMID 24386892not yet assessed
-
Manufacturing and Characterization of a Recombinant Adeno-Associated Virus Type 8 Reference Standard Material ↗Human Gene Therapy · 2014 · PMID 25275822not yet assessed
-
Recombinant adeno‐associated virus–mediated inhibition of microRNA‐21 protects mice against the lethal schistosome infection by repressing both IL‐13 and transforming growth factor beta 1 pathways ↗Hepatology · 2014 · PMID 25546547not yet assessed
-
Selective In Vivo Targeting of Human Liver Tumors by Optimized AAV3 Vectors in a Murine Xenograft Model ↗Human Gene Therapy · 2014 · PMID 25296041not yet assessed
-
Subretinal Delivery of AAV2-Mediated Human Erythropoietin Gene Is Protective and Safe in Experimental Diabetic Retinopathy ↗Investigative Ophthalmology & Visual Science · 2014 · PMID 24508793not yet assessed
-
Comparison of the efficacy of five adeno-associated virus vectors for transducing dorsal raphé nucleus cells in the mouse ↗Journal of Neuroscience Methods · 2014 · PMID 25046366not yet assessed
-
Making the White Matter Matters: Progress in Understanding Canavan’s Disease and Therapeutic Interventions Through Eight Decades ↗JIMD Reports · 2014 · PMID 25604619not yet assessed
-
Canavan?s disease as a model for development of efficacious, sustainable and safe rAAV gene therapeutics for CNS disordersJournal of Neurology & Neurophysiology · 2014not yet assessed
-
Inhibition of hepatocyte autophagy increases tumor necrosis factor-dependent liver injury by promoting caspase-8 activation ↗Cell Death and Differentiation · 2013 · PMID 23519075not yet assessed
-
Targeted Intraceptor Nanoparticle Therapy Reduces Angiogenesis and Fibrosis in Primate and Murine Macular Degeneration ↗ACS Nano · 2013 · PMID 23464925not yet assessed
-
Photoreceptor avascular privilege is shielded by soluble VEGF receptor-1 ↗eLife · 2013 · PMID 23795287not yet assessed
-
A Single Intravenous rAAV Injection as Late as P20 Achieves Efficacious and Sustained CNS Gene Therapy in Canavan Mice ↗Molecular Therapy · 2013 · PMID 23817205not yet assessed
-
Widespread spinal cord transduction by intrathecal injection of rAAV delivers efficacious RNAi therapy for amyotrophic lateral sclerosis ↗Human Molecular Genetics · 2013 · PMID 24108104not yet assessed
-
High-Efficiency Transduction of Primary Human Hematopoietic Stem Cells and Erythroid Lineage-Restricted Expression by Optimized AAV6 Serotype Vectors In Vitro and in a Murine Xenograft Model In Vivo ↗PLoS ONE · 2013 · PMID 23516552not yet assessed
-
Prefrontal Cortical Dysfunction After Overexpression of Histone Deacetylase 1 ↗Biological Psychiatry · 2013 · PMID 23664640not yet assessed
-
Recombinant Adeno-Associated Virus Integration Sites in Murine Liver After Ornithine Transcarbamylase Gene Correction ↗Human Gene Therapy · 2013 · PMID 23621841not yet assessed
-
Dicer expression is essential for adult midbrain dopaminergic neuron maintenance and survival ↗Molecular and Cellular Neuroscience · 2013 · PMID 24184162not yet assessed
-
Gene Transfer to the CNS Using Recombinant Adeno‐Associated Virus ↗Current Protocols in Microbiology · 2013 · PMID 23686825not yet assessed
-
Retinal Gene Delivery by rAAV and DNA Electroporation ↗Current Protocols in Microbiology · 2013 · PMID 23408132not yet assessed
-
Gene Transfer in Skeletal and Cardiac Muscle Using Recombinant Adeno‐Associated Virus ↗Current Protocols in Microbiology · 2013 · PMID 23408131not yet assessed
-
SU9518 Inhibits Proliferative Vitreoretinopathy in Fibroblast and Genetically Modified Müller Cell–Induced Rabbit Models ↗Investigative Ophthalmology & Visual Science · 2013 · PMID 23341018not yet assessed
-
Finding the Striatum in Sheep: Use of a Multi-Modal Guided Approach for Convection Enhanced Delivery ↗Journal of Huntington s Disease · 2013 · PMID 25063428not yet assessed
-
Gene Transfer in the Liver Using Recombinant Adeno‐Associated Virus ↗Current Protocols in Microbiology · 2013 · PMID 23686826not yet assessed
-
Gene Therapy for Canavan's Disease Takes a Step Forward ↗Molecular Therapy · 2013 · PMID 23449107not yet assessed
-
Vector Sequences Are Not Detected in Tumor Tissue from Research Subjects with Ornithine Transcarbamylase Deficiency Who Previously Received Adenovirus Gene Transfer ↗Human Gene Therapy · 2013 · PMID 24010702not yet assessed
-
Screening of Chinese herbal medicines against avian infectious laryngotracheitis virus and Escherichia coli.Agricultural Biotechnology · 2013not yet assessed
-
Histopathological observation of classical swine fever in newborn piglets.Agricultural Biotechnology · 2013not yet assessed
-
PCR detection of Streptococcus agalactiae in dairy cows suffering from mastitis.Agricultural Biotechnology · 2013not yet assessed
-
A single intravenous rAAV injection as late as P20 accomplishes efficacious and sustained CNS gene-therapy in a mouse model of Cananvan?s diseaseJournal of Neurology & Neurophysiology · 2013not yet assessed
-
Recombinant Vaccine to HIV-1 Gag A Simian Replication-Defective Adenoviral2013not yet assessed
-
not yet assessed
-
MabベースAC ELISAによる鶏IBDV分離株の抗原特性解析【Powered by NICT】Zhongguo shouyi xuebao · 2013not yet assessed
-
Vector Sequences Are Not Detected In Tumor Tissue From Research Subjects With Ornithine Transcarbamylase Deficiency Who Previously Received Adenovirus Gene Transfer ↗Human Gene Therapy · 2013not yet assessed
-
Histopathological observation of goose Escherichia coli disease.Agricultural Biotechnology · 2013not yet assessed
-
Effects of two drugs on small intestinal epithelial lymphocytes of experimental piglets with spleen deficiency.Agricultural Biotechnology · 2013not yet assessed
-
Long-term, efficient inhibition of microRNA function in mice using rAAV vectors ↗Nature Methods · 2012 · PMID 22388288not yet assessed
-
Production and Discovery of Novel Recombinant Adeno‐Associated Viral Vectors ↗Current Protocols in Microbiology · 2012 · PMID 22875565not yet assessed
-
Assessment of a passive immunity mouse model to quantitatively analyze the impact of neutralizing antibodies on adeno-associated virus-mediated gene transfer ↗Journal of Immunological Methods · 2012 · PMID 23063691not yet assessed
-
Hematology and Serum Chemistry Values in Adult Minks in Hebei Province, China ↗Journal of Animal and Veterinary Advances · 2012not yet assessed
-
Gene Transfer in the Lung Using Recombinant Adeno‐Associated Virus ↗Current Protocols in Microbiology · 2012 · PMID 22875566not yet assessed
-
Separation and identification of pathogens causing soft-shelled turtle fulminant infectious disease and preparation of anti-Aeromonas serum.Agricultural Science and Technology Hunan · 2012not yet assessed
-
PCR detection of virulence genes Colv, Stxs and HlyE of Escherichia coli.Agricultural Science and Technology Hunan · 2012not yet assessed
-
[HPA distribution characteristics of platelet donor population in Mudanjiang area of China and establishment of its database]. ↗PubMed · 2012 · PMID 22739197not yet assessed
-
Detection and sequence analysis of Escherichia coli virulence genes.Agricultural Science and Technology Hunan · 2012not yet assessed
-
Detection Class I Integron of Multidrug Resistace Pathogenic Salmonella from Chicken in Hebei Province, China ↗Journal of Animal and Veterinary Advances · 2012not yet assessed
-
Screening of Chinese herbal medicines resistant to chicken Escherichia coli and infectious laryngotracheitis virus.Agricultural Science and Technology Hunan · 2012not yet assessed
-
Detection of K88 Fimbriae Gene of Escherichia coli from MinkAnimal husbandry and feed science · 2012not yet assessed
-
Treatment efficacy of traditional Chinese veterinary medicine mycoplasma gallisepticum infection spray against experimental mycoplasma gallisepticum infection.Agricultural Science and Technology Hunan · 2012not yet assessed
-
Study on outer membrane protein patterns of Escherichia coli O38, O53 and O75 isolated from chickens.Agricultural Science and Technology Hunan · 2012not yet assessed
-
Analysis Of The Components And Clearance Of Retinal LipofuscinInvestigative Ophthalmology & Visual Science · 2012not yet assessed
-
Several rAAV Vectors Efficiently Cross the Blood–brain Barrier and Transduce Neurons and Astrocytes in the Neonatal Mouse Central Nervous System ↗Molecular Therapy · 2011 · PMID 21610699not yet assessed
-
The AAV9 receptor and its modification to improve in vivo lung gene transfer in mice ↗Journal of Clinical Investigation · 2011 · PMID 21576824not yet assessed
-
Inverse zonation of hepatocyte transduction with AAV vectors between mice and non-human primates ↗Molecular Genetics and Metabolism · 2011 · PMID 21778099not yet assessed
-
Cardiac Gene Transfer of Short Hairpin RNA Directed Against Phospholamban Effectively Knocks Down Gene Expression but Causes Cellular Toxicity in Canines ↗Human Gene Therapy · 2011 · PMID 21542669not yet assessed
-
Transendocardial Delivery of AAV6 Results in Highly Efficient and Global Cardiac Gene Transfer in Rhesus Macaques ↗Human Gene Therapy · 2011 · PMID 21563985not yet assessed
-
Evaluation of Adeno-Associated Viral Vectors for Liver-Directed Gene Transfer in Dogs ↗Human Gene Therapy · 2011 · PMID 21204705not yet assessed
-
Exploiting Natural Diversity of AAV for the Design of Vectors with Novel Properties ↗Methods in molecular biology · 2011 · PMID 22034027not yet assessed
-
Design of a Hydrologic Observation Database System ↗Communications in computer and information science · 2011not yet assessed
-
Correction: Single‐dose immunogenicity and protective efficacy of simian adenoviral vectors against Plasmodium berghei ↗European Journal of Immunology · 2011not yet assessed
-
MicroRNA-regulated, Systemically Delivered rAAV9: A Step Closer to CNS-restricted Transgene Expression ↗Molecular Therapy · 2010 · PMID 21179009not yet assessed
-
New Candidate Vaccines against Blood-StagePlasmodium falciparumMalaria: Prime-Boost Immunization Regimens Incorporating Human and Simian Adenoviral Vectors and Poxviral Vectors Expressing an Optimized Antigen Based on Merozoite Surface Protein 1 ↗Infection and Immunity · 2010 · PMID 20713623not yet assessed
-
Molecular Analysis of Vector Genome Structures After Liver Transduction by Conventional and Self-Complementary Adeno-Associated Viral Serotype Vectors in Murine and Nonhuman Primate Models ↗Human Gene Therapy · 2010 · PMID 20113166not yet assessed
-
Molecular characterization of adenoviruses in fecal samples of captively bred rhesus macaques in China ↗Veterinary Microbiology · 2010 · PMID 21215533not yet assessed
-
Transmission Electron Tomography of Adeno-Associated Virus (AAV) ↗Microscopy and Microanalysis · 2010not yet assessed
-
rAAV9--A Human-Derived Adeno-Associated Virus Vector for Efficient Transgene Expression in Mouse Cingulate Cortex: Figure 1. ↗Cold Spring Harbor Protocols · 2010 · PMID 20360371not yet assessed
-
Worldwide Epidemiology of Neutralizing Antibodies to Adeno‐Associated Viruses ↗The Journal of Infectious Diseases · 2009 · PMID 19133809not yet assessed
-
Adeno-Associated Virus-Mediated Gene Transfer to Nonhuman Primate Liver Can Elicit Destructive Transgene-Specific T Cell Responses ↗Human Gene Therapy · 2009 · PMID 19441963not yet assessed
-
Effect of Preexisting Immunity on an Adenovirus Vaccine Vector: In Vitro Neutralization Assays Fail To Predict Inhibition by Antiviral Antibody In Vivo ↗Journal of Virology · 2009 · PMID 19279092not yet assessed
-
Directed evolution of adeno-associated virus for glioma cell transduction ↗Journal of Neuro-Oncology · 2009 · PMID 19618115not yet assessed
-
Adenovirus–Adeno-Associated Virus Hybrid for Large-Scale Recombinant Adeno-Associated Virus Production ↗Human Gene Therapy · 2009 · PMID 19618999not yet assessed
-
not yet assessed
-
Adeno-Associated Virus (AAV) Serotype 9 Provides Global Cardiac Gene Transfer Superior to AAV1, AAV6, AAV7, and AAV8 in the Mouse and Rat ↗Human Gene Therapy · 2008 · PMID 18795839not yet assessed
-
Tailoring the AAV vector capsid for gene therapy ↗Gene Therapy · 2008 · PMID 19052631not yet assessed
-
The targeting of 14-succinate triptolide-lysozyme conjugate to proximal renal tubular epithelial cells ↗Biomaterials · 2008 · PMID 19100618not yet assessed
-
Single‐dose immunogenicity and protective efficacy of simian adenoviral vectors against Plasmodium berghei ↗European Journal of Immunology · 2008 · PMID 18266272not yet assessed
-
Percutaneous Transendocardial Delivery of Self-complementary Adeno-associated Virus 6 Achieves Global Cardiac Gene Transfer in Canines ↗Molecular Therapy · 2008 · PMID 18813281not yet assessed
-
Single-Dose Protection againstPlasmodium bergheiby a Simian Adenovirus Vector Using a Human Cytomegalovirus Promoter Containing Intron A ↗Journal of Virology · 2008 · PMID 18256155not yet assessed
-
Adenovirus-Based Vaccines Generate Cytotoxic T Lymphocytes to Epitopes of NS1 from Dengue Virus That Are Present in All Major Serotypes ↗Human Gene Therapy · 2008 · PMID 18788905not yet assessed
-
Novel Adenoviral Gene Delivery System Targeted Against Head and Neck Cancer ↗The Laryngoscope · 2008 · PMID 18176343not yet assessed
-
ADENOVIRUS BASED VACCINES GENERATE CYTOTOXIC T LYMPHOCYTES TO EPITOPES OF NS1 FROM DENGUE VIRUS THAT ARE PRESENT IN ALL MAJOR SEROTYPES ↗Human Gene Therapy · 2008not yet assessed
-
AAV9 Provides Global Cardiac Gene Transfer Superior to AAV1, AAV6, AAV7, and AAV8 in the Mouse and Rat ↗Human Gene Therapy · 2008not yet assessed
-
Adenovirus-based vaccine prevents pneumonia in ferrets challenged with the SARS coronavirus and stimulates robust immune responses in macaques ↗Vaccine · 2007 · PMID 17559989not yet assessed
-
A CD46-binding Chimpanzee Adenovirus Vector as a Vaccine Carrier ↗Molecular Therapy · 2007 · PMID 17228314not yet assessed
-
Heparin binding directs activation of T cells against adeno-associated virus serotype 2 capsid ↗Nature Medicine · 2006 · PMID 16845388not yet assessed
-
Analysis of Tumors Arising in Male B6C3F1 Mice with and without AAV Vector Delivery to Liver ↗Molecular Therapy · 2006 · PMID 16682254not yet assessed
-
Structure-Based Identification of a Major Neutralizing Site in an Adenovirus Hexon ↗Journal of Virology · 2006 · PMID 17108028not yet assessed
-
High-Level Transgene Expression in Nonhuman Primate Liver with Novel Adeno-Associated Virus Serotypes Containing Self-Complementary Genomes ↗Journal of Virology · 2006 · PMID 16731960not yet assessed
-
Long-Term Correction of Ammonia Metabolism and Prolonged Survival in Ornithine Transcarbamylase-Deficient Mice Following Liver-Directed Treatment with Adeno-associated Viral Vectors ↗Molecular Therapy · 2006 · PMID 16677864not yet assessed
-
A Common Mechanism for Cytoplasmic Dynein-Dependent Microtubule Binding Shared among Adeno-Associated Virus and Adenovirus Serotypes ↗Journal of Virology · 2006 · PMID 16840360not yet assessed
-
Complete Prevention of Atherosclerosis in ApoE-Deficient Mice by Hepatic Human ApoE Gene Transfer With Adeno-Associated Virus Serotypes 7 and 8 ↗Arteriosclerosis Thrombosis and Vascular Biology · 2006 · PMID 16763161not yet assessed
-
Efficacy of Severe Acute Respiratory Syndrome Vaccine Based on a Nonhuman Primate Adenovirus in the Presence of Immunity Against Human Adenovirus ↗Human Gene Therapy · 2006 · PMID 16716107not yet assessed
-
Identification of Novel Adeno-Associated Virus Serotypes for Use as Vectors ↗Elsevier eBooks · 2006not yet assessed
-
Corrigendum to “Biology of AAV Serotype Vectors in Liver-Directed Gene Transfer to Nonhuman Primates” ↗Molecular Therapy · 2006 · PMID 28192691not yet assessed
-
206. Frequency and Analysis of Liver Tumors in AAV-Treated B6C3F1 Hybrid Mice ↗Molecular Therapy · 2006not yet assessed
-
744. Novel Vectors for Gene Therapy: Covering the Spectrum of Primate AAV Diversity ↗Molecular Therapy · 2006not yet assessed
-
609. Acute-Phase Toxicity Following Systemic Administration of Non-Human Primate Derived Adenoviral Vectors to Mice ↗Molecular Therapy · 2006not yet assessed
-
77. TLR and Myd88 Signaling Pathway Is Required for the Full Induction of Host Adaptive Immune Responses to Adenoviral Vectors and Transgenes ↗Molecular Therapy · 2006not yet assessed
-
Efficacy of Severe Acute Respiratory Syndrome Vaccine Based on a Nonhuman Primate Adenovirus in the Presence of Immunity Against Human Adenovirus ↗Human Gene Therapy · 2006not yet assessed
-
Contributors ↗Elsevier eBooks · 2006not yet assessed
-
New Recombinant Serotypes of AAV Vectors ↗Current Gene Therapy · 2005 · PMID 15975006not yet assessed
-
Identification of murine CD8 T cell epitopes in codon-optimized SARS-associated coronavirus spike protein ↗Virology · 2005 · PMID 15823604not yet assessed
-
Biology of AAV Serotype Vectors in Liver-Directed Gene Transfer to Nonhuman Primates ↗Molecular Therapy · 2005 · PMID 16219492not yet assessed
-
High Levels of Persistent Expression of α1-Antitrypsin Mediated by the Nonhuman Primate Serotype rh.10 Adeno-associated Virus Despite Preexisting Immunity to Common Human Adeno-associated Viruses ↗Molecular Therapy · 2005 · PMID 16260185not yet assessed
-
Chimpanzee adenovirus vaccine protects against Zaire Ebola virus ↗Virology · 2005 · PMID 16356525not yet assessed
-
Evaluation of toxicity from high-dose systemic administration of recombinant adenovirus vector in vector-naïve and pre-immunized mice ↗Gene Therapy · 2005 · PMID 15647774not yet assessed
-
Chimpanzee-origin adenovirus vectors as vaccine carriers ↗Gene Therapy · 2005 · PMID 16319951not yet assessed
-
An optimized protocol for detection of E. coli β-galactosidase in lung tissue following gene transfer ↗Histochemistry and Cell Biology · 2005 · PMID 15947941not yet assessed
-
In vivo targeting of vaccinating tumor cells to antigen-presenting cells by a gene therapy method with adenovirus containing the α1,3galactosyltransferase gene ↗Cancer Gene Therapy · 2005 · PMID 15818383not yet assessed
-
A tctex1-Ca2+ channel complex for selective surface expression of Ca2+ channels in neurons ↗Nature Neuroscience · 2005 · PMID 15768038not yet assessed
-
Elimination of rheumatoid synovium in situusing a Fas ligand 'gene scalpel' ↗Arthritis Research & Therapy · 2005 · PMID 16277676not yet assessed
-
Innate Immune Responses to Adenoviral Vector-Mediated Acute Pancreatitis ↗Pancreas · 2005 · PMID 15714134not yet assessed
-
Oral Vaccination of Mice with Adenoviral Vectors Is Not Impaired by Preexisting Immunity to the Vaccine Carrier ↗Journal of Virology · 2005not yet assessed
-
Clades of Adeno-Associated Viruses Are Widely Disseminated in Human Tissues ↗Journal of Virology · 2004 · PMID 15163731not yet assessed
-
Long-term pharmacologically regulated expression of erythropoietin in primates following AAV-mediated gene transfer ↗Blood · 2004 · PMID 15507527not yet assessed
-
Resolution of Primary Severe Acute Respiratory Syndrome-Associated Coronavirus Infection Requires Stat1 ↗Journal of Virology · 2004 · PMID 15452265not yet assessed
-
Gene therapy with novel adeno‐associated virus vectors substantially diminishes atherosclerosis in a murine model of familial hypercholesterolemia ↗The Journal of Gene Medicine · 2004 · PMID 15170737not yet assessed
-
Characterization of a Family of Chimpanzee Adenoviruses and Development of Molecular Clones for Gene Transfer Vectors ↗Human Gene Therapy · 2004 · PMID 15144581not yet assessed
-
Proteasome Inhibition Enhances AAV-Mediated Transgene Expression in Human Synoviocytes in Vitro and in Vivo ↗Molecular Therapy · 2004 · PMID 15771962not yet assessed
-
Complete nucleotide sequences and genome organization of four chimpanzee adenoviruses ↗Virology · 2004 · PMID 15207622not yet assessed
-
Human Immunodeficiency Virus Type 1-Specific Immune Responses in Primates upon Sequential Immunization with Adenoviral Vaccine Carriers of Human and Simian Serotypes ↗Journal of Virology · 2004 · PMID 15220412not yet assessed
-
Novel adenoviral vectors coding for GFP-tagged wtCFTR and ?F508-CFTR: characterization of expression and electrophysiological properties in A549 cells ↗Pflügers Archiv - European Journal of Physiology · 2004 · PMID 15452712not yet assessed
-
Recombinant adeno-associated virus preferentially transduces human, compared to mouse, synovium: implications for arthritis therapy ↗Modern Rheumatology · 2004 · PMID 17028800not yet assessed
-
Recombinant adeno-associated virus preferentially transduces human, compared to mouse, synovium: implications for arthritis therapy ↗Modern Rheumatology · 2004not yet assessed
-
Fatal systemic inflammatory response syndrome in a ornithine transcarbamylase deficient patient following adenoviral gene transfer ↗Molecular Genetics and Metabolism · 2003 · PMID 14567964not yet assessed
-
Adeno-associated viruses undergo substantial evolution in primates during natural infections ↗Proceedings of the National Academy of Sciences · 2003 · PMID 12716974not yet assessed
-
Erythropoietin gene therapy leads to autoimmune anemia in macaques ↗Blood · 2003 · PMID 14695227not yet assessed
-
A Simian Replication-Defective Adenoviral Recombinant Vaccine to HIV-1 Gag ↗The Journal of Immunology · 2003 · PMID 12538702not yet assessed
-
Total correction of hemophilia A mice with canine FVIII using an AAV 8 serotype ↗Blood · 2003 · PMID 14551134not yet assessed
-
AAV2 Vector Harboring a Liver-Restricted Promoter Facilitates Sustained Expression of Therapeutic Levels of α-Galactosidase A and the Induction of Immune Tolerance in Fabry Mice ↗Molecular Therapy · 2003 · PMID 14759807not yet assessed
-
Oral Vaccination of Mice with Adenoviral Vectors Is Not Impaired by Preexisting Immunity to the Vaccine Carrier ↗Journal of Virology · 2003 · PMID 14512528not yet assessed
-
Regulated expression of erythropoietin from an AAV vector safely improves the anemia of β-thalassemia in a mouse model ↗Molecular Therapy · 2003 · PMID 12727112not yet assessed
-
Mucosally Delivered E1-Deleted Adenoviral Vaccine Carriers Induce Transgene Product-Specific Antibody Responses in Neonatal Mice ↗The Journal of Immunology · 2003 · PMID 14530353not yet assessed
-
Induction of CD8+ T cells to an HIV-1 antigen upon oral immunization of mice with a simian E1-deleted adenoviral vector ↗Vaccine · 2003 · PMID 14741162not yet assessed
-
Efficient Transduction of Human Monocyte-Derived Dendritic Cells by Chimpanzee-Derived Adenoviral Vector ↗Human Gene Therapy · 2003 · PMID 12718764not yet assessed
-
T Helper Cell-Independent Antibody Responses to the Transgene Product of an E1-Deleted Adenoviral Vaccine Require NK1.1 T Cells ↗Virology · 2003 · PMID 12573585not yet assessed
-
Novel adeno-associated viruses from rhesus monkeys as vectors for human gene therapy ↗Proceedings of the National Academy of Sciences · 2002 · PMID 12192090not yet assessed
-
A Pilot Study of In Vivo Liver-Directed Gene Transfer with an Adenoviral Vector in Partial Ornithine Transcarbamylase Deficiency ↗Human Gene Therapy · 2002 · PMID 11779420not yet assessed
-
Novel, Chimpanzee Serotype 68-Based Adenoviral Vaccine Carrier for Induction of Antibodies to a Transgene Product ↗Journal of Virology · 2002 · PMID 11861833not yet assessed
-
Preexisting Immunity to Adenovirus in Rhesus Monkeys Fails To Prevent Vector-Induced Toxicity ↗Journal of Virology · 2002 · PMID 11991999not yet assessed
-
Rep/Cap Gene Amplification and High-Yield Production of AAV in an A549 Cell Line Expressing Rep/Cap ↗Molecular Therapy · 2002 · PMID 11991756not yet assessed
-
Noninvasive gene transfer to the lung for systemic delivery of therapeutic proteins ↗Journal of Clinical Investigation · 2002 · PMID 12189244not yet assessed
-
Chimpanzee adenovirus CV-68 adapted as a gene delivery vector interacts with the coxsackievirus and adenovirus receptor ↗Journal of General Virology · 2002 · PMID 11752711not yet assessed
-
Noninvasive gene transfer to the lung for systemic delivery of therapeutic proteins ↗Journal of Clinical Investigation · 2002not yet assessed
-
A New Scalable Method for the Purification of Recombinant Adenovirus Vectors ↗Human Gene Therapy · 2002 · PMID 12427304not yet assessed
-
Noninvasive gene transfer to the lung for systemic delivery of therapeutic proteins ↗Journal of Clinical Investigation · 2002not yet assessed
-
Acute Cytokine Response to Systemic Adenoviral Vectors in Mice Is Mediated by Dendritic Cells and Macrophages ↗Molecular Therapy · 2001 · PMID 11356075not yet assessed
-
Activation of Innate Immunity in Nonhuman Primates Following Intraportal Administration of Adenoviral Vectors ↗Molecular Therapy · 2001 · PMID 11356076not yet assessed
-
Sequestration of Adenoviral Vector by Kupffer Cells Leads to a Nonlinear Dose Response of Transduction in Liver ↗Molecular Therapy · 2001 · PMID 11162308not yet assessed
-
Isolation of Highly Infectious and Pure Adeno-Associated Virus Type 2 Vectors with a Single-Step Gravity-Flow Column ↗Human Gene Therapy · 2001 · PMID 11177544not yet assessed
-
Replication-Defective Vector Based on a Chimpanzee Adenovirus ↗Journal of Virology · 2001 · PMID 11689642not yet assessed
-
Hybrid Vectors Based on Adeno-Associated Virus Serotypes 2 and 5 for Muscle-Directed Gene Transfer ↗Journal of Virology · 2001 · PMID 11390622not yet assessed
-
Muscle-Specific Promoters May Be Necessary for Adeno-Associated Virus-Mediated Gene Transfer in the Treatment of Muscular Dystrophies ↗Human Gene Therapy · 2001 · PMID 11177557not yet assessed
-
Biology of E1-Deleted Adenovirus Vectors in Nonhuman Primate Muscle ↗Journal of Virology · 2001 · PMID 11333904not yet assessed
-
Adeno-associated virus preferentially transduces human compared to mouse synovium ↗Arthritis Research · 2001not yet assessed
-
Purification of Recombinant Adeno-Associated Virus Vectors by Column Chromatography and Its Performance in Vivo ↗Human Gene Therapy · 2000 · PMID 11044910not yet assessed
-
CD40 Ligand-Dependent Activation of Cytotoxic T Lymphocytes by Adeno-Associated Virus Vectors In Vivo: Role of Immature Dendritic Cells ↗Journal of Virology · 2000 · PMID 10933709not yet assessed
-
Adeno-Associated Virus Mediates Long-Term Gene Transfer and Delivery of Chondroprotective IL-4 to Murine Synovium ↗Molecular Therapy · 2000 · PMID 10947942not yet assessed
-
Prolonged Correction of Hyperlipidemia in Mice with Familial Hypercholesterolemia Using an Adeno-Associated Viral Vector Expressing Very-Low-Density Lipoprotein Receptor ↗Molecular Therapy · 2000 · PMID 10985956not yet assessed
-
A Cell Line for High-Yield Production of E1-Deleted Adenovirus Vectors without the Emergence of Replication-Competent Virus ↗Human Gene Therapy · 2000 · PMID 10646652not yet assessed
-
Production of recombinant adeno-associated virus ↗Advances in virus research · 2000 · PMID 11050955not yet assessed
-
Electron Microscopic Evaluation of Vector Quality for Gene Therapy ↗Microscopy and Microanalysis · 2000not yet assessed
-
Gene Therapy Vectors Based on Adeno-Associated Virus Type 1 ↗Journal of Virology · 1999 · PMID 10196295not yet assessed
-
Stable transgene expression in rod photoreceptors after recombinant adeno-associated virus-mediated gene transfer to monkey retina ↗Proceedings of the National Academy of Sciences · 1999 · PMID 10449795not yet assessed
-
Regulated Delivery of Therapeutic Proteins After in Vivo Somatic Cell Gene Transfer ↗Science · 1999 · PMID 9872748not yet assessed
-
Repeated Administration of Adenoviral Vectors in Lungs of Human CD4 Transgenic Mice Treated with a Nondepleting CD4 Antibody ↗The Journal of Immunology · 1999 · PMID 10384148not yet assessed
-
Overexpression of Cyclin A Inhibits Augmentation of Recombinant Adeno-Associated Virus Transduction by the Adenovirus E4orf6 Protein ↗Journal of Virology · 1999 · PMID 10559315not yet assessed
-
5 Adenovirus Vectors ↗Cold Spring Harbor Monograph Archive · 1999not yet assessed
-
High-Titer Adeno-Associated Viral Vectors from a Rep/Cap Cell Line and Hybrid Shuttle Virus ↗Human Gene Therapy · 1998 · PMID 9829534not yet assessed
-
Role of E4 in Eliciting CD4 T-Cell and B-Cell Responses to Adenovirus Vectors Delivered to Murine and Nonhuman Primate Lungs ↗Journal of Virology · 1998 · PMID 9621078not yet assessed
-
Comparative toxicity of E4 deleted vectors expressing human ornithine transcarbamylase (OTC) cDNA ♦ 730 ↗Pediatric Research · 1998not yet assessed
-
Biology of adenovirus vectors with E1 and E4 deletions for liver-directed gene therapy ↗Journal of Virology · 1996 · PMID 8971023not yet assessed
-
Molecular studies of Canavan DiseaseFlorida International University Digital Commons (Florida International University) · 1994not yet assessed
-
Transcriptional Analysis of Bm-1 Repetitive Elements in the genome of Bombvx moriFlorida International University Digital Commons (Florida International University) · 1991not yet assessed
Full bibliography from OpenAlex; reproducibility verdicts matched by PMID.
Author attribution follows OpenAlex disambiguation, which is imperfect — a researcher's papers can be split across profiles or mixed with a namesake.
Merged across profiles sharing this ORCID where present. See every “Gao G” paper on PubMed ↗